An experimental gene therapy for a rare form of genetic deafness has successfully restored hearing in children and adults, ...

An estimated 170,000 Australians were diagnosed with cancer in 2025. Many people know the causes of cancer are partly genetic. But how do your genes, which contribute so much of what makes you you, ...

Key Takeaways Otarmeni, a gene therapy targeting a specific mutation that causes profound deafness, now has U.S. Food and ...

The gene editing treatment targets the relatively common 1717-1G>A splicing mutation, which does not respond to many current ...

A new study from the Massachusetts Institute of Technology suggests that a specific gene mutation prevents patients with schizophrenia from updating their understanding of reality. Researchers found ...

An estimated 170,000 Australians were diagnosed with cancer in 2025. Many people know the causes of cancer are partly genetic. But how do your genes, which contribute so much of what makes you you, ...

Nerve cells made from an iPS cell of an autism patient with a mutation in the POGZ gene (right, green). The number is fewer than those of a non-autistic person (left). (Photos courtesy of Osaka ...

A genetic mutation that helps animals like yaks and Tibetan antelopes survive at high altitudes may hold the key to repairing nerve damage in conditions such as cerebral paralysis and multiple ...

For roughly one in ten people living with cystic fibrosis, the drugs that have transformed survival for most CF patients are ...

One of the symptoms of schizophrenia is difficulty incorporating new information about the world. This can lead people with schizophrenia to struggle with making decisions and, eventually, to lose ...